The Use of CRISPR- Cas Has Revolutionized the Gene Therapy

question 4

Multiple Choice

The use of CRISPR- cas has revolutionized the gene therapy field.One of the first uses of CRISPR- cas to edit genes in vivo was done at MIT.What disease did they cure?

• A)B- thalassemia
• B)RDEB
• C)type 1 tyrosinemia
• D)HIV

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Definitions:

Dehydration

Dehydration is a condition that occurs when the body loses more fluids than it takes in, leading to a deficiency in the amount of water and electrolytes.

Attention Deficit Hyperactivity Disorder

A neurodevelopmental disorder characterized by problems with focus, hyperactivity, and impulsiveness which are not appropriate for a person's age.

Cerebral Palsy

A group of permanent movement disorders that appear in early childhood, caused by abnormal brain development or damage to the developing brain.

Down Syndrome

A genetic disorder caused by the presence of all or part of a third copy of chromosome 21, characterized by intellectual disability, distinctive facial features, and possible health complications.