Treatment of Lysosomal Storage Diseases with Enzyme Replacement Therapy Involves

question 31

Multiple Choice

Treatment of lysosomal storage diseases with enzyme replacement therapy involves _______.

• A)sending functional copies of the missing enzyme to the precise cell sites where the deficiency is manifested
• B)targeting mutant copies of the missing enzyme to the cell sites where the deficiency is manifested
• C)targeting functional copies of another enzyme to the cell sites where the deficiency is manifested
• D)administration of small molecular weight drugs to inhibit the synthesis of substances that accumulate in the disease
• E)administration of large molecular weight drugs to inhibit the synthesis of substances that accumulate in the disease

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Definitions:

Second Stage

Refers to a subsequent phase or step in a process or sequence, often implying development or progression from an initial stage.

Dilations

The process of expansion or enlargement in geometry, or the widening of blood vessels or pupils in biological contexts.

Actual Birth

The occurrence or process of being born.

Contractions

The tightening and shortening of muscles, often referring to those of the uterus during childbirth.