Why Is Duchenne Muscular Dystrophy (DMD) a Technically Difficult Disease

question 13

Multiple Choice

Why is Duchenne muscular dystrophy (DMD) a technically difficult disease to treat with gene therapy?

• A) The DMD gene is too repetitive
• B) It will be difficult to target the vector to enough myocytes to be therapeutic
• C) DMD uses multiple promoters in different cell types
• D) DMD has complicated alternative splicing patterns
• E) B and C

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Definitions:

Processed Further

A term in cost accounting referring to additional operations or processing steps applied to a product after the initial manufacturing phase.

Crushing Process

A method in material processing where large pieces are reduced to smaller sizes, often used in mining and waste management.

Industrial Fiber

Engineered fibers used in manufacturing for their specific properties, such as strength, flexibility, or resistance to heat.

Joint Process

A manufacturing procedure in which multiple products are produced simultaneously from the same raw materials or processes.