What Modification Has Increased the Success of Enzyme Replacement Therapy

question 6

Multiple Choice

What modification has increased the success of enzyme replacement therapy for Gaucher disease?

• A) Using larger doses of enzyme
• B) Targeting the enzyme to cross the blood-brain barrier
• C) Modifying the enzyme so that it is targeted to macrophage lysosomes
• D) Providing the enzyme in conjunction with a bone marrow transplant
• E) Removal of the spleen before treatment

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