Why Might a Patient with ADA-SCID Be a Good Candidate

question 37

Multiple Choice

Why might a patient with ADA-SCID be a good candidate for somatic cell gene therapy?
1) The ADA gene was one of the first human disease genes to be cloned and characterized.
2) White blood cells can easily be obtained from ADA - SCID patients and reintroduced after functional copies of the ADA gene are added
3) Even a small amount of functional ADA will restore partial immune function

• A) 1
• B) 2
• C) 3
• D) 1 and 2
• E) All of these