Treatment of Lysosomal Storage Diseases with Enzyme Replacement Therapy Involves

question 117

Multiple Choice

Treatment of lysosomal storage diseases with enzyme replacement therapy involves _______.

• A)targeting functional copies of the missing enzyme to the precise cell sites where the deficiency is manifested
• B)targeting mutant copies of the missing enzyme to the cell sites where the deficiency is manifested
• C)targeting functional copies of another enzyme to the cell sites where the deficiency is manifested
• D)administration of small molecular weight drugs to inhibit the synthesis of substances that accumulate in the disease
• E)administration of large molecular weight drugs to inhibit the synthesis of substances that accumulate in the disease

---

Definitions:

Market Power

The ability of a firm or group of firms to influence the price of a good or service in the market, often through controlling supply, demand, or both.

Inefficiency

Occurs when resources are not used in the most effective way, resulting in wasted resources or lost opportunities, often identified in markets with monopolies or restrictive trade practices.

Imperfectly Competitive Industry

A market structure characterized by a few producers that have some control over the price and where products are differentiated.

Control Over Price

The ability of a person or entity to influence the market price of a product or service.