Treatment of Lysosomal Storage Disorders with Substrate Reduction Therapy Involves

question 32

Multiple Choice

Treatment of lysosomal storage disorders with substrate reduction therapy involves _______.

• A)targeting functional copies of the missing enzyme to the cell sites where the deficiency is manifested
• B)targeting mutant copies of the missing enzyme to the cell sites where the deficiency is manifested
• C)targeting functional copies of another enzyme to the cell sites where the deficiency is manifested
• D)administration of small molecular weight drugs to inhibit the synthesis of the substances that accumulate in the disease
• E)administration of large molecular weight drugs to inhibit the synthesis of the substances that accumulate in the disease

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Definitions:

Direct Method

A cash flow statement preparation approach that lists major classes of gross cash receipts and payments.

Gain

A financial term referring to the positive difference between the sale price of an asset and its original purchase price.

Financing Activities

Transactions that result in changes in the size and composition of the equity capital or borrowings of the company.

Stockholders' Equity

The residual interest in the assets of an entity that remains after deducting its liabilities, representing ownership equity in a corporation.